Home » EMA Grants BioMarin Priority Medicine Support for Hemophilia Therapy
EMA Grants BioMarin Priority Medicine Support for Hemophilia Therapy
BioMarin received a priority medicine designation from the European Medicines Agency for its gene therapy treatment for hemophilia A.
The therapy, BMN 270, is designed to alter a genetic problem by adding a corrected copy of the defective gene. In this case, it would be factor VIII, a clotting protein.
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